Gene Therapy Stocks
Biotechnology firms in this sector focus on the permanent modification of patient genetic material to treat or cure hereditary diseases and chronic conditions at their molecular source.
As of Oct 23, 2026, Gene Therapy has 56 US-listed companies worth $194B combined. The median member moved -0.7% over the past week; TSHA led among the 25 largest at +9.4% and SLBT trailed at -24.8%.
Companies in Gene Therapy
- VRTX – Vertex Pharmaceuticals Inc, $136B
- RGEN – Repligen Corporation, $11.3B
- KRYS – Krystal Biotech Inc, $9.6B
- PTCT – PTC Therapeutics Inc, $5.3B
- CRSP – Crispr Therapeutics AG, $4.8B
- BEAM – Beam Therapeutics Inc, $2.5B
- MRVI – Maravai Lifesciences Holdings Inc, $2.4B
- PGEN – Precigen Inc, $2.3B
- SRPT – Sarepta Therapeutics Inc, $1.8B
- NTLA – Intellia Therapeutics Inc, $1.6B
- QURE – Uniqure NV, $1.6B
- RARE – Ultragenyx, $1.6B
- TSHA – Taysha Gene Therapies Inc, $1.4B
- MGTX – MeiraGTx Holdings PLC, $955M
- SLBT – SL Science Holding Limited Ordinary Shares, $869M
- SANA – Sana Biotechnology Inc, $835M
- SLDB – Solid Biosciences LLC, $737M
- DSGN – Design Therapeutics Inc, $732M
- FDMT – 4D Molecular Therapeutics Inc, $711M
- CADL – Candel Therapeutics Inc, $709M
- PRME – Prime Medicine, Inc. Common Stock, $707M
- RGNX – Regenxbio Inc, $473M
- TKNO – Alpha Teknova Inc, $468M
- EDIT – Editas Medicine Inc, $445M
- NGNE – Neurogene Inc, $431M
- SCTX – Scribe Therapeutics Inc. Common Stock, $380M
- BNTC – Benitec Biopharma Ltd ADR, $335M
- IRD – Opus Genetics, Inc., $318M
- CLPT – Clearpoint Neuro Inc, $277M
- OCGN – Ocugen Inc, $265M
- ABEO – Abeona Therapeutics Inc, $252M
- RCKT – Rocket Pharmaceuticals Inc, $239M
- LXEO – Lexeo Therapeutics, Inc. Common Stock, $217M
- CAMP – CAMP4 THERAPEUTICS CORPORATION, $215M
- DTIL – Precision BioSciences Inc, $173M
- KRRO – Korro Bio, Inc., $141M
- CLLS – Cellectis SA, $135M
- ENGN – enGene Holdings Inc. Common Stock, $119M
- VYGR – Voyager Therapeutics Inc, $117M
- PLYX – Polaryx Therapeutics, Inc. Common Stock, $98.2M
- TNYA – Tenaya Therapeutics Inc, $87.5M
- CRBU – Caribou Biosciences Inc, $50.4M
- MGX – Metagenomi, Inc. Common Stock, $37.8M
- GNTA – Genenta Science SpA ADR, $34.8M
- GUTS – Fractyl Health, Inc. Common Stock, $20.6M
- PASG – Passage Bio Inc, $11.9M
- PHIO – Phio Pharmaceuticals Corp, $10.9M
- SNTI – Senti Biosciences Inc, $7.1M
- LNAI – Lunai Bioworks Inc., $6.3M
- ORGS – Orgenesis Inc, $3.4M
- MBIO – Mustang Bio Inc, $3.1M
- GOVX – GeoVax Labs Inc, $2.9M
- GNPX – Genprex Inc, $1.7M
- SCPS – Scopus Biopharma Inc, $16,833
- THMO – Thermogenesis Holdings Inc, $1,584
- FIXX – Homology Medicines Inc